World’s first personalized CRISPR therapy given to baby with genetic disease

A baby boy with a devastating genetic disease is thriving after becoming the first known person to receive a bespoke, CRISPR therapy-for-one, designed to correct his specific disease-causing mutation.

Little KJ Muldoon, now nearly ten months old, is doing well after receiving three doses of a gene-editing treatment 

Read the full article here.

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